CORRAO, Federica
CORRAO, Federica
Scienze e Tecnologie Biologiche Chimiche e Farmaceutiche
A precision medicine approach to primary immunodeficiency disease: Ataluren strikes nonsense mutations once again
2025-03-29 Laura Lentini; Riccardo Perriera; Federica Corrao; Raffaella Melfi; Marco Tutone; Pietro Carollo; Ignazio Fiduccia; Andrea Pace; Davide Ricci; Francesco Genovese; Alain Colige; Philippe Delvenne; Bodo Grimbacher; Michel Moutschen; Ivana Pibiri
Aging modifies receptor expression but not muscular contractile response to angiotensin II in rat jejunum
2022-11-01 Zizzo, Maria Grazia; Cicio, Adele; Corrao, Federica; Lentini, Laura; Serio, Rosa
CFTR G542X/ G542X mouse model carrying nonsense mutations, useful tool to test the efficacy of translational readthrough-based therapy in Cystic Fibrosis
Federica Corrao, Emanuele Vitale, Maria Grazia Zizzo, Raffaella Melfi, Ignazio Fiduccia, Davide Ricci, Marco Tutone, Andrea Pace, Aldo di Leonardo, Ivana Pibiri, Laura Lentini
Evaluation of the biodistribution and activity of new optimized readthrough molecules in Cystic fibrosis mouse model and other model systems
2023-12-11
Inhibition of FTSJ1, a tryptophan tRNA-specific 2’-O-methyltransferase as possible mechanism to readthrough premature termination codons (UGAs) of the CFTR mRNA
2022-09-01 Pietro Salvatore Carollo; Marco Tutone; Riccardo Perriera; Rossella Rizzo; Federica Corrao; Ivana Pibiri; Aldo Di Leonardo; Maria Grazia Zizzo; Andrea Pace; Laura Lentini
Investigating the inhibition of FTSJ1 a tryptophan tRNA-specific 2’-O-methyltransferase by NV TRIDs, as a mechanism of readthrough in nonsense mutated CFTR
2023-06-01 Pietro Salvatore Carollo; Marco Tutone; Giulia Culletta; Ignazio Fiduccia; Federica Corrao; Ivana Pibiri; Maria Grazia Zizzo; Raffaella Melfi; Andrea Pace; Anna Maria Almerico; Laura Lentini
Nonsense codons suppression. An acute toxicity study of three optimized TRIDs in murine model, safety and tolerability evaluation
2022-12-01 Corrao, Federica; Zizzo, Maria Grazia; Tutone, Marco; Melfi, Raffaella; Fiduccia, Ignazio; Carollo, Pietro Salvatore; Leonardo, Aldo Di; Caldara, Gaetano; Perriera, Riccardo; Pace, Andrea; Belmonte, Beatrice; Sammataro, Selene; Pibiri, Ivana; Lentini, Laura
P015 Translational readthrough inducing drugs: a study of toxicity in mice models and in vitro safety validation of the specific readthrough process.
2022-06-08 Federica Corrao, Riccardo Perriera, Laura Lentini, Maria Grazia Zizzo, Raffaella Melfi, Pietro Salvatore Carollo, Ignazio Fiduccia, Andrea Pace, Marco Tutone, Aldo Di Leonardo, Ivana Pibiri.
Production of CHM R293X cell model system to study the rescue of the Rab Escort Protein-1 expression by TRIDs nonsense suppression activity
2023-09-01 Emanuele Vitale, Raffaella Melfi, Federica Corrao, Ignazio Fiduccia, Davide Ricci, Ivana Pibiri, Andrea Pace, Laura Lentini
Promoting readthrough of nonsense mutations in CF mouse model: Biodistribution and efficacy of NV848 in rescuing CFTR protein expression
2024-01-01 Fiduccia I.; Corrao F.; Zizzo M.G.; Perriera R.; Genovese F.; Vitale E.; Ricci D.; Melfi R.; Tutone M.; Pace A.; Lentini L.; Pibiri I.
Readthrough Approach Using NV Translational Readthrough-Inducing Drugs (TRIDs): A Study of the Possible Off-Target Effects on Natural Termination Codons (NTCs) on TP53 and Housekeeping Gene Expression
2023-10-11 Perriera, Riccardo; Vitale, Emanuele; Pibiri, Ivana; Carollo, Pietro Salvatore; Ricci, Davide; Corrao, Federica; Fiduccia, Ignazio; Melfi, Raffaella; Zizzo, Maria Grazia; Tutone, Marco; Pace, Andrea; Lentini, Laura
Readthrough Inducing Drugs (TRIDs) in human fibroblasts harboring the c.5047 C>T (R1683*) nonsense mutation
2022-09-01 Federica Corrao, Raffaella Melfi, Marco Tutone, Ignazio Fiduccia, Riccardo Perriera, Pietro Salvatore Carollo, Emanuele Vitale, Andrea Pace, Laura Lentini, A. Colige, P. Delvenne, B. Grimbacher, M. Moutschen, I. Pibiri
RESCUE OF LRBA GENE EXPRESSION IN PRIMARY HUMAN FIBROBLASTS CHARACTERISED BY NONSENSE MUTATION c. 5047 (C>T).
2021-04-22 Riccardo PERRIERA, Federica CORRAO, Ivana PIBIRI, Andrea PACE, Laura LENTINI
The innovative role of the readthrough inducing drugs in the translation rescue of mRNAs characterized by premature stop codon (PTCs).
Translational Readthrough Inducing Drugs (TRIDs): a study of biodistribution evaluation in mice models
I. Fiduccia, F. Corrao, R. Perriera, A. Di Leonardo, R. Melfi, A. Pace, M. Tutone, M.G. Zizzo, L. Lentini, I. Pibiri
Unlocking Cellular Secrets: Charting Proteomic Frontiers in LRBA Deficiency Through the Lens of Readthrough Promoters
I. Fiduccia, D. Ricci, F. Corrao, E. Vitale, R. Melfi, A. Pace, M. Tutone, M.G. Zizzo, L. Lentini, I. Pibiri, Michel Moutschen, Samuel Meier-Menches