FIDUCCIA, IGNAZIO
FIDUCCIA, IGNAZIO
Scienze e Tecnologie Biologiche Chimiche e Farmaceutiche
A precision medicine approach for nonsense mutations: study of novel small molecules for the rescue of p53 protein expression
Vitale, E.; Menditto, M.; Ricci, D.; Carollo, P.S.; Fiduccia, I.; Varrica, R.; Cruciata, I.; Melfi, R.; Pace, A.; Pibiri, I.; Cooperman, B.S.; Lentini, L.
A precision medicine approach to primary immunodeficiency disease: Ataluren strikes nonsense mutations once again
2025-03-29 Laura Lentini; Riccardo Perriera; Federica Corrao; Raffaella Melfi; Marco Tutone; Pietro Carollo; Ignazio Fiduccia; Andrea Pace; Davide Ricci; Francesco Genovese; Alain Colige; Philippe Delvenne; Bodo Grimbacher; Michel Moutschen; Ivana Pibiri
A study on molecules promoting the readthrough of nonsense mutations (TRIDs)
2024-12-18
Beyond Nonsense: New Molecules as Precision Therapy for Rare Genetic Diseases
Pibiri, I.; Ricci, D.; Fiduccia, I.; Tutone, M.; Culletta, G.; Cruciata, I.; Menditto, M.; Subhan, F.; Varrica, R.; Vitale, E.; Rizzo, C.; Marino, S.; Melfi, R.; Zizzo, M.G.; Lentini, L.
CFTR G542X/ G542X mouse model carrying nonsense mutations, useful tool to test the efficacy of translational readthrough-based therapy in Cystic Fibrosis
Federica Corrao, Emanuele Vitale, Maria Grazia Zizzo, Raffaella Melfi, Ignazio Fiduccia, Davide Ricci, Marco Tutone, Andrea Pace, Aldo di Leonardo, Ivana Pibiri, Laura Lentini
CFTR rescue in a G542X nonsense mouse model of cystic fibrosis: investigating the mechanism of action and activity of translational readthrough-inducing drugs
2025-06-01 Vitale, E.; Cruciata, I.; Varrica, R.; Fiduccia, I.; Tutone, M.; Menditto, M.; Ricci, D.; Melfi, R.; Pibiri, I.; Pace, A.; Zizzo, M.G.; Cooperman, B.S.; Lentini, L.
Functionalization of Biobased Polymers: Synthesis, Characterization and Environmental Applications
Rizzo, C.; Ricci, D.; Fiduccia, I.; Maio, A.; Scaffaro, R.; Pace, A.; Pibiri, I.
Identification of New Translational Readthrough Inducing Drugs
Investigating the inhibition of FTSJ1 a tryptophan tRNA-specific 2’-O-methyltransferase by NV TRIDs, as a mechanism of readthrough in nonsense mutated CFTR
2023-06-01 Carollo, P.S.; Tutone, M.; Culletta, G.; Fiduccia, I.; Corrao, F.; Pibiri, I.; Zizzo, M.G.; Melfi, R.; Pace, A.; Almerico, A.M.; Lentini, L.
Nonsense codons suppression. An acute toxicity study of three optimized TRIDs in murine model, safety and tolerability evaluation
2022-12-01 Corrao, Federica; Zizzo, Maria Grazia; Tutone, Marco; Melfi, Raffaella; Fiduccia, Ignazio; Carollo, Pietro Salvatore; Leonardo, Aldo Di; Caldara, Gaetano; Perriera, Riccardo; Pace, Andrea; Belmonte, Beatrice; Sammataro, Selene; Pibiri, Ivana; Lentini, Laura
Nonsense Mutations in Rare and Ultra-Rare Human Disorders: An Overview
2025-06-06 Vitale, E.; Ricci, D.; Corrao, F.; Fiduccia, I.; Cruciata, I.; Carollo, P.; Branchini, A.; Lentini, L.; Pibiri, I.
P015 Translational readthrough inducing drugs: a study of toxicity in mice models and in vitro safety validation of the specific readthrough process.
2022-06-08 Federica Corrao, Riccardo Perriera, Laura Lentini, Maria Grazia Zizzo, Raffaella Melfi, Pietro Salvatore Carollo, Ignazio Fiduccia, Andrea Pace, Marco Tutone, Aldo Di Leonardo, Ivana Pibiri.
Potential translational readthough inducin drugs: an optimized design and synthesis of new chemical scaffolds
Davide Ricci; Giulia Culletta; Marco Tutone; Ignazio Fiduccia; Emanuele Vitale; Carla Rizzo; Pietro Salvatore Carollo; Raffaella Melfi; Maria Grazia Zizzo; Laura Lentini; Ivana Pibiri
Production of CHM R293X cell model system to study the rescue of the Rab Escort Protein-1 expression by TRIDs nonsense suppression activity
2023-09-01 Emanuele Vitale, Raffaella Melfi, Federica Corrao, Ignazio Fiduccia, Davide Ricci, Ivana Pibiri, Andrea Pace, Laura Lentini
Promoting readthrough of nonsense mutations in CF mouse model: Biodistribution and efficacy of NV848 in rescuing CFTR protein expression
2024-01-01 Fiduccia I.; Corrao F.; Zizzo M.G.; Perriera R.; Genovese F.; Vitale E.; Ricci D.; Melfi R.; Tutone M.; Pace A.; Lentini L.; Pibiri I.
Readthrough Approach Using NV Translational Readthrough-Inducing Drugs (TRIDs): A Study of the Possible Off-Target Effects on Natural Termination Codons (NTCs) on TP53 and Housekeeping Gene Expression
2023-10-11 Perriera, Riccardo; Vitale, Emanuele; Pibiri, Ivana; Carollo, Pietro Salvatore; Ricci, Davide; Corrao, Federica; Fiduccia, Ignazio; Melfi, Raffaella; Zizzo, Maria Grazia; Tutone, Marco; Pace, Andrea; Lentini, Laura
Readthrough Inducing Drugs (TRIDs) in human fibroblasts harboring the c.5047 C>T (R1683*) nonsense mutation
2022-09-01 Federica Corrao, Raffaella Melfi, Marco Tutone, Ignazio Fiduccia, Riccardo Perriera, Pietro Salvatore Carollo, Emanuele Vitale, Andrea Pace, Laura Lentini, A. Colige, P. Delvenne, B. Grimbacher, M. Moutschen, I. Pibiri
Rescuing nonsense in cancer: recovering p53 tumor suppressor gene expression by translational readthrough inducing drugs (TRIDs)
2025-06-15 Laura Lentini, Michele Menditto, Davide Ricci, Pietro Salvatore Carollo, Emanuele Vitale, Ignazio Fiduccia, Ilenia Cruciata, Raffaella Melfi, Ivana Pibiri
Shaping 1,2,4-Triazolium Fluorinated Ionic Liquid Crystals
2023-02-24 Rizzo C.; Fiduccia I.; Buscemi S.; Palumbo Piccionello A.; Pace A.; Pibiri I.
Translational readthrough approach to fight nonsense in cancer: design and synthesis of new trids rescuing P53