: In adults with SMA, risdiplam therapy may improve respiratory function. In these patients, sniff nasal inspiratory pressure is the most effective test to demonstrate effects of pharmacological therapy. https://bit.ly/3Wk2MCU.

Crescimanno, G., Alonge, P., Lupica, A., Tomasello, V., Di Stefano, V., Brighina, F., et al. (2026). Evaluating effects of risdiplam in adults with spinal muscular atrophy: a monocentric study. ERJ OPEN RESEARCH, 12(2), 1-4 [10.1183/23120541.01120-2025].

Evaluating effects of risdiplam in adults with spinal muscular atrophy: a monocentric study

Alonge, Paolo;Lupica, Antonino;Di Stefano, Vincenzo;Brighina, Filippo;
2026-03-01

Abstract

: In adults with SMA, risdiplam therapy may improve respiratory function. In these patients, sniff nasal inspiratory pressure is the most effective test to demonstrate effects of pharmacological therapy. https://bit.ly/3Wk2MCU.
mar-2026
Crescimanno, G., Alonge, P., Lupica, A., Tomasello, V., Di Stefano, V., Brighina, F., et al. (2026). Evaluating effects of risdiplam in adults with spinal muscular atrophy: a monocentric study. ERJ OPEN RESEARCH, 12(2), 1-4 [10.1183/23120541.01120-2025].
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Utilizza questo identificativo per citare o creare un link a questo documento: https://hdl.handle.net/10447/711463
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